Issue: April 2017
A UCSF initiative aims to use high-throughput sequencing of pediatric tumors – including whole genome and RNA sequencing – to identify new therapeutic targets for pediatric cancers with high death rates.
Issue: January 2017
Gene editing technology and clinical expertise enabled researchers to correct the genetic mutation that causes sickle cell disease in stem cells. Clinical trials will likely follow soon.
A phase II study tests a novel immunotherapy that uses patients’ own immune cells to protect cells that produce insulin.
Issue: September 2017
Combining in-utero hematopoietic stem cell transplant with a fetal transfusion of red blood cells tests theory that fetus is unlikely to reject the mother’s stem cells within a certain stage of the pregnancy
The UCSF-led Pacific Pediatric Neuro-Oncology Consortium (PNOC) clinical trials have begun to yield encouraging results for children with brain tumors.